A 2-Part, Randomized, Double-Blind, Placebo-Controlled Study in Participants with Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping with an Initial Multiple Ascending Dose Part A to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ENTR-601-44, Followed by Part B to Evaluate the Safety and Efficacy of ENTR-601-44 (ELEVATE-44) (ENTR-601-44-201 (ELEVATE-44))
Principal Investigator
Prof Laurent Servais
Contact us
Email: childrensresearch@ouh.nhs.uk
IRAS number
1010840